Session 4: Manfred Schmidt Memorial Session

11:45-12:00  Christof von Kalle, Charité, Berlin Institute of Health

Introduction

INV11    12:00-12:30 

Alain Fischer, Necker-Enfants Malades Hospital, Paris  ⓘ

Long term analysis of gene therapy for SCID and related diseases

INV12    12:30-13:00 

David Williams, Harvard Medical School, Boston  ⓘ

Flipping the switch; post-transcriptional genetic silencing of BCL11A to treat Sickle Cell Disease

ABSTRACT >